BTK Inhibitor Shows Potential in Early Phase Trial for MS
August 15th 2018A phase 1 trial evaluating the safety and tolerability of PRN2246, a Bruton's tyrosine kinase (BTK) inhibitor, found the drug having no serious medication-related adverse events in healthy volunteers while also being able to reach the brain.
Read More
First Targeted Treatment of Polyneuropathy in Rare Disease Wins FDA Approval
August 10th 2018Patisiran (Onpattro, Alnylam Pharmaceuticals) is indicated for the treatment of adult patients with polyneuropathy caused by hereditary transthyretin-mediated amyloidosis (hATTR), a rare genetic disease.
Read More