|Videos|April 19, 2021

Living with and Treatment Options for Spinal Muscular Atrophy

Pharmacy Times spoke with spinal muscular atrophy (SMA) patient Nick Sinagra about his treatment journey and his experiences with 2 different SMA treatments.

Sinagra discussed his experiences using SPINRAZA and Evrysdi, the challenges of living with SMA, what pharmacists need to understand about counseling patients with SMA, and what he hopes to see for the future of the rare disease.

Stay informed on drug updates, treatment guidelines, and pharmacy practice trends—subscribe to Pharmacy Times for weekly clinical insights.

Subscribe Now!

Latest CME

Virtual Symposium Registration

Metabolic Drivers of MASLD/MASH: Understanding the Disease and Identifying At-Risk Patients

Tuesday, May 12, 2026 | 1:00 PM – 2:00 PM EDT

Virtual Event

Diabetes Day of Education 2026

Thursday, May 14, 2026

Virtual Event

Bridging Gaps in Meningococcal Protection: Pharmacist-Led Approaches to Vaccination and Public Health Equity

Tuesday, May 19, 2026 | 1:00 PM – 2:30 PM EDT

Virtual Event

Cardiology Day of Education 2026

Thursday, June 4, 2026

Virtual Event

Cardiology Day of Education 2026

Thursday, June 4, 2026

Living with and Treatment Options for Spinal Muscular Atrophy

Newsletter

Related Content

From Misdiagnosis to Advocacy: Addressing Bias and Equity in Heart Failure Management

Amid Mounting Pressure, FDA Commissioner Marty Makary to Resign

Managing ASCVD: Where Patients and Clinicians Still Need Help

Q&A: Pharmacist-Led Strategies to Help Improve Diabetes Outcomes and Lower Costs

Polycystic Ovary Syndrome Undergoes Name Change: Polyendocrine Metabolic Ovarian Syndrome

Latest CME

Metabolic Drivers of MASLD/MASH: Understanding the Disease and Identifying At-Risk Patients

Diabetes Day of Education 2026

Bridging Gaps in Meningococcal Protection: Pharmacist-Led Approaches to Vaccination and Public Health Equity

Cardiology Day of Education 2026

Cardiology Day of Education 2026

A Deep Dive Into CGM Data

Advancements With CGM Integrations: Insulin Pumps, Connected Pens, and Ketone Monitoring

Immunology Specialty Pharmacy Day of Education 2026

Stimulant Stewardship: A Pharmacist’s Guide to ADHD Prescribing During Drug Shortages

Directions in Pharmacy 2026

Not All Bispecifics Are Equal: Mechanism-Based Approaches to Selection and Management in Oncology Practice

From Evidence to Access: Integrating SGLT2 Inhibitors Across the Cardiorenal-Metabolic Continuum

The Educated Pharmacist: Using Patient Insights to Personalize Insulin Therapy and Prevent Clinical Inertia

From Flares to Freedom: Navigating the Journey of Patients With Chronic Spontaneous Urticaria With Next-Generation Therapies

Understanding Type 2 Inflammation and Its Role Across Various Immune-Related Diseases

Innovations in Lymphoma Treatment and the Growing Impact of Bispecific Antibodies

Advancing Pharmacist Expertise in R/R FL: Navigating Novel Therapies and Optimizing Patient Outcomes

Optimizing Outcomes in Myasthenia Gravis: Therapeutic Advances and Value-Based Care Models

Navigating Novel Therapies in Steroid-Refractory cGVHD: Practical Strategies for Community-Based Oncology Pharmacists

Reducing Transfusion Burden in Myeloid Disorders: Novel Therapeutic Strategies and Pharmacist Interventions

Clinical Panel Debate: CAR T-Cell Therapy vs Bispecific Antibodies

From Molecules to Medicine: Pharmacologic Principles of Innovative Non-Hodgkin Lymphoma Therapies

Understanding mRNA Vaccines: Dispelling Myths and Empowering Pharmacists to Counsel Patients

Precision Matters: Foundations of Biomarker-Driven Care in Non-Small Cell Lung Cancer

Navigating the Legal Landscape of Telehealth: Updates and Implications for Pharmacists and Technicians (Pharmacy Technician Credit)

Navigating the Legal Landscape of Telehealth: Updates and Implications for Pharmacists and Technicians

Clinical Presentation of Hyperglycemia with PI3K and AKT Inhibitors

Reducing the Treatment Burden in HIV Management: The Pharmacist’s Role in Long-Acting Injectable Adoption

Optimizing Lipid Management in Statin-Intolerant Populations: Payer Strategies for Evidence-Based Access and Risk Reduction

Protecting Against Meningococcal Disease: Updates on Vaccines, Guidelines, and Pharmacist Best Practices

Targeting the Root of Autoimmunity in Generalized Myasthenia Gravis: Pharmacist Strategies for Integrating FcRn Therapies Into Specialty Practice

IL-23 Inhibitors in Psoriasis: Optimizing Access and Patient Outcomes Across Integrated Systems

Utilizing VMAT-2 Inhibitors for the Management of Tardive Dyskinesia: The Role of Long-Term Care Pharmacists

Influenza Immunization in Older Adults: Enhanced Vaccines and Best Practices for Long-Term Care Pharmacists

Effective Strategies to Manage Hyperglycemia When Treating with PI3K and AKT Inhibitors

Cardiorenal Protection With SGLT2 Inhibitors: Perspectives for Managed Care

Bridging Innovation and Access in HR-Positive/HER2-Negative Metastatic Breast Cancer: Implications for Managed Care

Navigating Advanced Prostate Cancer Treatment: Optimizing Novel Therapeutic Strategies for Managed Care Pharmacists

Multidisciplinary Insights to Enhance Biomarker Testing Practices in Non-Small Cell Lung Cancer

Treating MASH in 2026: Guideline-Directed Care and Emerging Therapeutic Strategies

Diabetes Day of Education 2026

Evolving Care: Treating Demodex Blepharitis for Pharmacists

Navigating the Metabolic MASH-Up: Integrating Screening Modalities and Specialty Pharmacotherapy in MASLD Care

Implementing Pharmacist-Led Strategies to Support Comprehensive MASH Management

Improving the Care of Persons Living With Diabetes Using CGM Devices (Pharmacy Technician Credit)

Improving the Care of Persons Living With Diabetes Using CGM Devices

Demystifying CGM: Addressing Frequently Asked Questions and Key Insights

Advancing Stroke Prevention: The Pharmacist’s Role in Implementing the 2024 Guidelines

From Guidelines to Practice: The Pharmacist’s Role in Chronic Heart Failure Therapy Optimization

Mastering Hyperlipidemia Management: Enhancing Adherence and Expanding Nonstatin Therapy Options

Beyond the Prescription: Tackling Social Isolation for Better Health (Pharmacy Technician Credit)

Discipline Decoded: Navigating Pharmacy Law and Disciplinary Cases

Balancing Pain Management and Opioid Use Disorder: Recognition, Treatment, and Compassionate Communication in Pharmacy Practice

Beyond the Prescription: Tackling Social Isolation for Better Health

Evaluating the Role of Pharmacists in Utilizing Potassium-Competitive Acid Blockers for Acid Peptic Disorders

Understanding and Personalizing Chronic Obstructive Pulmonary Disease Diagnosis and Treatment

Empowering Pharmacists in Travel Medicine: Enhancing Patient Care Through Vaccination, Prevention, and Education (Pharmacy Technician Credit)

Discipline Decoded: Navigating Pharmacy Law and Disciplinary Cases (Pharmacy Technician Credit)

Empowering Pharmacists in Travel Medicine: Enhancing Patient Care Through Vaccination, Prevention, and Education

Leveraging Novel Therapies to Transform Demodex Blepharitis Care (Pharmacy Technician Credit)

Leveraging Novel Therapies to Transform Demodex Blepharitis Care

Advancing Multiple Sclerosis Treatment: Exploring Evolving Therapies and Patient-Centered Approaches

New and Emerging Therapies for the Management of Narcolepsy: A Guide to Patient-Centered Care

Navigating the Complexity of Migraine: A Multimodal Approach to Acute Treatment

Identifying and Personalizing Iron Deficiency Anemia Treatment in Patients With Cancer

Managing Iron Replacement Therapies for Patients With Inflammatory Bowel Disease

Iron Deficiency Anemia Treatment Considerations in Women’s Health

The Changing Paradigm in Pain Management and Supporting Access to Novel Therapies

Exploring ATTR Phenotypes and Identifying Appropriate Opportunities for Pharmacists to Intervene

Personalizing Treatment in Relapsed/Refractory Multiple Myeloma: The Evolving Role of Antibody-Drug Conjugates and Bispecific Antibodies

Advances in Castration-Sensitive Prostate Cancer: A Pharmacist's Approach to Optimize Novel Antiandrogen Therapies